1区 · 综合性期刊
ArticleOA
作者: Kashani-Sabet, Mohammed ; Chmura, Stephen A. ; Handumrongkul, Chakkrapong ; Debs, Robert ; Mack, Marissa ; Ursu, Sarah J. ; Lewis, David B. ; Thistle, Robert ; Heath, Timothy D. ; Liu, Yong ; Ye, Alice L. ; Soroceanu, Liliana ; Liggitt, Denny ; Ice, Ryan J. ; Myers, Methawee
HEDGES, a tunable nonviral DNA-based gene therapy platform, durably expresses human therapeutic proteins in immunocompetent mice.