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项与 CRISPR/Cas9 modified human haematopoietic stem cell therapy (Allife Medical Science and Technology) 相关的临床试验A Safety and Efficacy Study of a Single Center, Open-label, Single Arm About the Gene Correction of HBB in Patient-specific iHSCs Using CRISPR/Cas9 That Intervent Subjests With β-thalassemia Mutations
This is a single centre、single arm、open-label study,to investigate the safety and efficacy of the gene correction of HBB in patient-specific iHSCs using CRISPR/Cas9.
100 项与 CRISPR/Cas9 modified human haematopoietic stem cell therapy (Allife Medical Science and Technology) 相关的临床结果
100 项与 CRISPR/Cas9 modified human haematopoietic stem cell therapy (Allife Medical Science and Technology) 相关的转化医学
100 项与 CRISPR/Cas9 modified human haematopoietic stem cell therapy (Allife Medical Science and Technology) 相关的专利(医药)
100 项与 CRISPR/Cas9 modified human haematopoietic stem cell therapy (Allife Medical Science and Technology) 相关的药物交易