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项与 COL7A1 gene-modified autologous fibroblasts 相关的临床试验Phase I Study of Lentiviral-mediated COL7A1 Gene-modified Autologous Fibroblasts in Adults With Recessive Dystrophic Epidermolysis Bullosa.
Recessive dystrophic epidermolysis bullosa (RDEB) is a severe form of blistering skin disease caused by mutations in COL7A1 gene. This study aims to assess the safety of intradermal injections of gene-modified autologous fibroblasts in 5-10 adults with RDEB.
100 项与 COL7A1 gene-modified autologous fibroblasts 相关的临床结果
100 项与 COL7A1 gene-modified autologous fibroblasts 相关的转化医学
100 项与 COL7A1 gene-modified autologous fibroblasts 相关的专利(医药)
100 项与 COL7A1 gene-modified autologous fibroblasts 相关的药物交易